Drugs that target a gene either directly (oncogene) or via a synthetic-lethal partner (SLP) of a mutated tumour suppressor (TSG). Cell colour shows the strongest known status of that drug for that cancer subtype: approved clinical trial repositionable (potential reuse, no evidence yet) or blank.
| Drug | TSG | SLP (drug target) | GBM | LUAD | SCLC | LUSC | OAC | OSCC | PDAC | # |
|---|---|---|---|---|---|---|---|---|---|---|
| neo212 oral capsule, ipilimumab, pembrolizumab, nivolumab, regorafenib, carboplatin, paclitaxel, folfiri protocol, bevacizumab | DICER1 | DDR2 | 4 | |||||||
| regorafenib, (stivarga, bay73-4506), nivolumab (opdivo) | DICER1 | DDR2 | 4 | |||||||
| adavosertib, afatinib, afatinib dimaleate, binimetinib, biopsy, biospecimen collection, capivasertib, computed tomography, copanlisib, copanlisib hydrochloride, crizotinib, cytology specimen collection procedure, dabrafenib, dabrafenib mesylate, dasatinib, defactinib, defactinib hydrochloride, echocardiography, erdafitinib, fexagratinib, ipatasertib, laboratory biomarker analysis, larotrectinib, larotrectinib sulfate, magnetic resonance imaging, multigated acquisition scan, nivolumab, osimertinib, palbociclib, pertuzumab, pi3k-beta inhibitor gsk2636771, radiologic examination, radionuclide imaging, relatlimab, sapanisertib, sunitinib malate, taselisib, trametinib, trastuzumab, trastuzumab emtansine, ulixertinib, vismodegib | DICER1 | SRC | 3 | |||||||
| adavosertib, afatinib, afatinib dimaleate, binimetinib, biopsy, biospecimen collection, capivasertib, computed tomography, copanlisib, copanlisib hydrochloride, crizotinib, cytology specimen collection procedure, dabrafenib, dabrafenib mesylate, dasatinib, defactinib, defactinib hydrochloride, echocardiography, erdafitinib, fexagratinib, ipatasertib, laboratory biomarker analysis, larotrectinib, larotrectinib sulfate, magnetic resonance imaging, multigated acquisition scan, nivolumab, osimertinib, palbociclib, pertuzumab, pi3k-beta inhibitor gsk2636771, radiologic examination, radionuclide imaging, relatlimab, sapanisertib, sunitinib malate, taselisib, trametinib, trastuzumab, trastuzumab emtansine, ulixertinib, vismodegib | DICER1 | CSK | 3 | |||||||
| nivolumab or pembrolizumab (dependent upon approved indication), metformin, rosiglitazone | DICER1 | PPARD | 3 | |||||||
| regorafenib | DICER1 | DDR2 | 7 | |||||||
| bevacizumab, dasatinib, fluorouracil, leucovorin, leucovorin calcium, oxaliplatin, quality-of-life assessment | DICER1 | SRC | 2 | |||||||
| bevacizumab, dasatinib, fluorouracil, leucovorin, leucovorin calcium, oxaliplatin, quality-of-life assessment | DICER1 | CSK | 2 | |||||||
| bryostatin 1, paclitaxel | DICER1 | TNF | 2 | |||||||
| bryostatin 1, paclitaxel | DICER1 | PRKCA | 2 | |||||||
| fluorouracil, irinotecan hydrochloride, leucovorin calcium, vorinostat, pharmacological study | DICER1 | HDAC2 | 2 | |||||||
| motexafin gadolinium, radiation therapy | DICER1 | RRM2 | 2 | |||||||
| nintedanib | DICER1 | SRC | 2 | |||||||
| nintedanib, pembrolizumab | DICER1 | SRC | 2 | |||||||
| pembrolizumab, guadecitabine, mocetinostat | DICER1 | HDAC2 | 2 | |||||||
| pharmacological study, romidepsin | DICER1 | HDAC2 | 2 | |||||||
| pharmacological study, romidepsin | DICER1 | HDAC4 | 2 | |||||||
| regorafenib, laboratory biomarker analysis | DICER1 | DDR2 | 2 | |||||||
| rituximab | DICER1 | MS4A1 | 2 | |||||||
| vinorelbine, cisplatin, vinorelbine, cisplatin, radiotherapy | DICER1 | TUBB | 2 | |||||||
| bethanechol | DICER1 | CHRM1 | 7 | |||||||
| bosutinib | DICER1 | SRC | 7 | |||||||
| carfilzomib | DICER1 | PSMB8 | 7 | |||||||
| romidepsin | DICER1 | HDAC2 | 7 | |||||||
| vinorelbine | DICER1 | TUBB | 7 | |||||||
| 3-dimensional conformal radiation therapy, cognitive assessment, laboratory biomarker analysis, temozolomide, vorinostat | DICER1 | HDAC2 | 1 | |||||||
| 3-dimensional conformal radiation therapy, intensity-modulated radiation therapy (imrt), temozolomide, chloroquine, tumor treating fields therapy (ttf) | DICER1 | TNF | 1 | |||||||
| 3-dimensional conformal radiation therapy, intensity-modulated radiation therapy, laboratory biomarker analysis, vorinostat | DICER1 | HDAC2 | 1 | |||||||
| 3-dimensional conformal radiation therapy, motexafin gadolinium, temozolomide | DICER1 | RRM2 | 1 | |||||||
| adjuvant therapy, temozolomide, valproic acid, radiation therapy | DICER1 | HDAC2 | 1 | |||||||
| adjuvant therapy, temozolomide, valproic acid, radiation therapy | DICER1 | HDAC9 | 1 | |||||||
| adjuvant therapy, temozolomide, valproic acid, radiation therapy | DICER1 | PPARD | 1 | |||||||
| adriamycin, cyclophosphamide, vindesine, valproic acid | DICER1 | HDAC2 | 1 | |||||||
| adriamycin, cyclophosphamide, vindesine, valproic acid | DICER1 | HDAC9 | 1 | |||||||
| adriamycin, cyclophosphamide, vindesine, valproic acid | DICER1 | PPARD | 1 | |||||||
| afatinib, dasatinib, palbociclib, everolimus, olaparib | DICER1 | SRC | 1 | |||||||
| afatinib, dasatinib, palbociclib, everolimus, olaparib | DICER1 | CSK | 1 | |||||||
| atorvastatin, temozolomide, radiotherapy | DICER1 | HDAC2 | 1 | |||||||
| azacitidine, vorinostat, gemcitabine, busulfan, melphalan, dexamethasone, caphosol, glutamine, pyridoxine, rituximab | DICER1 | HDAC2 | 1 | |||||||
| azacitidine, vorinostat, gemcitabine, busulfan, melphalan, dexamethasone, caphosol, glutamine, pyridoxine, rituximab | DICER1 | MS4A1 | 1 | |||||||
| bethanechol, gemcitabine, nab-paclitaxel | DICER1 | CHRM1 | 1 | |||||||
| bevacizumab, dasatinib, placebo | DICER1 | SRC | 1 | |||||||
| bevacizumab, dasatinib, placebo | DICER1 | CSK | 1 | |||||||
| bevacizumab, temozolomide, vorinostat | DICER1 | HDAC2 | 1 | |||||||
| byl719, poziotinib, nintedanib, abemaciclib, durvalumab,tremelimumab | DICER1 | SRC | 1 | |||||||
| canakinumab, tislelizumab, nab-paclitaxel, gemcitabine | DICER1 | IL1B | 1 | |||||||
| capecitabine, vorinostat, radiotherapy, surgery to remove tumor | DICER1 | HDAC2 | 1 | |||||||
| ce-mark approved laa closure devices, acetylsalicylic acid, clopidogrel, dabigatran, rivaroxaban, apixaban, edoxaban, phenprocoumon, warfarin | DICER1 | MYC | 1 | |||||||
| chemotherapy, cladribine, radiation therapy | DICER1 | RRM2 | 1 | |||||||
| chloroquine | DICER1 | TNF | 1 | |||||||
| chloroquine, radiotherapy, temozolomide | DICER1 | TNF | 1 | |||||||
| chlorpromazine, temozolomide, radiation therapy | DICER1 | CHRM1 | 1 | |||||||
| concomitant temozolomide (tmz), radiotherapy, procarbazine, adjuvant temozolomide (tmz), ccnu, vincristine | DICER1 | TUBB | 1 | |||||||
| conventional surgery, 3-dimensional conformal radiation therapy, stereotactic radiosurgery, motexafin gadolinium, magnetic resonance imaging, spectroscopy | DICER1 | RRM2 | 1 | |||||||
| cytoreductive surgery, perifosine, temsirolimus | DICER1 | PRKCA | 1 | |||||||
| dabrafenib, trametinib, carboplatin, vincristine | DICER1 | TUBB | 1 | |||||||
| dasatinib, erlotinib hydrochloride, gemcitabine hydrochloride | DICER1 | SRC | 1 | |||||||
| dasatinib, erlotinib hydrochloride, gemcitabine hydrochloride | DICER1 | CSK | 1 | |||||||
| dasatinib, gemcitabine hydrochloride, laboratory biomarker analysis, mutation analysis, nucleic acid sequencing, immunohistochemistry staining method | DICER1 | SRC | 1 | |||||||
| dasatinib, gemcitabine hydrochloride, laboratory biomarker analysis, mutation analysis, nucleic acid sequencing, immunohistochemistry staining method | DICER1 | CSK | 1 | |||||||
| dasatinib, laboratory biomarker analysis, physiologic testing | DICER1 | SRC | 1 | |||||||
| dasatinib, laboratory biomarker analysis, physiologic testing | DICER1 | CSK | 1 | |||||||
| dasatinib, mfolfox6 | DICER1 | SRC | 1 | |||||||
| dasatinib, mfolfox6 | DICER1 | CSK | 1 | |||||||
| dasatinib, pharmacological study | DICER1 | SRC | 1 | |||||||
| dasatinib, pharmacological study | DICER1 | CSK | 1 | |||||||
| dasatinib, temozolomide, placebo, radiation therapy | DICER1 | SRC | 1 | |||||||
| dasatinib, temozolomide, placebo, radiation therapy | DICER1 | CSK | 1 | |||||||
| depatuxizumab mafodotin, temozolomide, lomustine | DICER1 | TUBB | 1 | |||||||
| dexanabinol | DICER1 | TNF | 1 | |||||||
| disulfiram, copper, alkylating agents | DICER1 | TKT | 1 | |||||||
| disulfiram, copper, alkylating agents | DICER1 | TUBB | 1 | |||||||
| disulfiram, copper, alkylating agents | DICER1 | P4HB | 1 | |||||||
| disulfiram, copper, alkylating agents | DICER1 | HSP90AA1 | 1 | |||||||
| docetaxel, cisplatin, radiation, surgery, vinorelbine, cisplatin | DICER1 | TUBB | 1 | |||||||
| etanercept, tocilizumab | DICER1 | TNF | 1 | |||||||
| etomidate, midazolam, meperidine | DICER1 | CHRM1 | 1 | |||||||
| farletuzumab, placebo, carboplatin, paclitaxel, pemetrexed, cisplatin | DICER1 | FOLR1 | 1 | |||||||
| gemcitabine hydrochloride, tanespimycin | DICER1 | HSP90AA1 | 1 | |||||||
| gemcitabine, etanercept | DICER1 | TNF | 1 | |||||||
| gemcitabine, oxaliplatin, imatinib | DICER1 | DDR2 | 1 | |||||||
| gemcitabine, sorafenib, vorinostat, 3-dimensional conformal radiation therapy, intensity-modulated radiation therapy, rosettesep, depfff | DICER1 | HDAC2 | 1 | |||||||
| gemcitabine, vinorelbine, cisplatin, etoposide, carboplatin | DICER1 | TUBB | 1 | |||||||
| imatinib, irinotecan, carboplatin | DICER1 | DDR2 | 1 | |||||||
| imexon, gemcitabine | DICER1 | RRM2 | 1 | |||||||
| irinotecan, cisplatin, simvastatin | DICER1 | HDAC2 | 1 | |||||||
| ketamine, ketamine injectable product, meaning and purpose therapy, placebo, questionnaires | DICER1 | CHRM1 | 1 | |||||||
| laboratory biomarker analysis, perifosine, temsirolimus, therapeutic conventional surgery | DICER1 | PRKCA | 1 | |||||||
| laboratory biomarker analysis, pharmacological study, temozolomide, vorinostat | DICER1 | HDAC2 | 1 | |||||||
| mebendazole, vincristine, carboplatin, temozolomide, bevacizumab, irinotecan | DICER1 | TUBB | 1 | |||||||
| medical cannabis | DICER1 | IDO1 | 1 | |||||||
| medical cannabis | DICER1 | NAAA | 1 | |||||||
| medical cannabis | DICER1 | SOD1 | 1 | |||||||
| minocycline, placebo, questionnaires | DICER1 | IL1B | 1 | |||||||
| motexafin gadolinium | DICER1 | RRM2 | 1 | |||||||
| motexafin gadolinium, magnetic resonance imaging, surgical procedure | DICER1 | RRM2 | 1 | |||||||
| nabiximols, temozolomide, nabiximols-matched placebo | DICER1 | IDO1 | 1 | |||||||
| nabiximols, temozolomide, nabiximols-matched placebo | DICER1 | NAAA | 1 | |||||||
| nabiximols, temozolomide, nabiximols-matched placebo | DICER1 | SOD1 | 1 | |||||||
| paclitaxel, bryostatin 1 | DICER1 | TNF | 1 | |||||||
| paclitaxel, bryostatin 1 | DICER1 | PRKCA | 1 | |||||||
| patupilone | DICER1 | TUBB | 1 | |||||||
| pembrolizumab, vorinostat, temozolomide, radiotherapy | DICER1 | HDAC2 | 1 | |||||||
| pemetrexed, cetuximab, cisplatin, folic acid, vitamin b12 | DICER1 | FOLR1 | 1 | |||||||
| perifosine | DICER1 | PRKCA | 1 | |||||||
| ponatinib | DICER1 | SRC | 1 | |||||||
| recombinant interferon alfa-2b, cisplatin, sodium stibogluconate, dacarbazine, vinblastine | DICER1 | TUBB | 1 | |||||||
| regorafenib, lomustine | DICER1 | DDR2 | 1 | |||||||
| regorafenib, nivolumab, capeox, folfox regimen | DICER1 | DDR2 | 1 | |||||||
| regorafenib, nivolumab, docetaxel, paclitaxel, irinotecan, trifluridine/tipracil | DICER1 | DDR2 | 1 | |||||||
| regorafenib, temozolomide | DICER1 | DDR2 | 1 | |||||||
| romidepsin | DICER1 | HDAC4 | 1 | |||||||
| romidepsin, azacitidine, nab-paclitaxel, gemcitabine, durvalumab, lenalidomide capsule | DICER1 | HDAC2 | 1 | |||||||
| romidepsin, azacitidine, nab-paclitaxel, gemcitabine, durvalumab, lenalidomide capsule | DICER1 | HDAC4 | 1 | |||||||
| romidepsin, laboratory biomarker analysis | DICER1 | HDAC2 | 1 | |||||||
| romidepsin, laboratory biomarker analysis | DICER1 | HDAC4 | 1 | |||||||
| selinexor, temozolomide, generic radiation therapy (rt), selective serotonin receptor (5-ht3) antagonists, olanzapine, salt tablets, anti-diarrheal | DICER1 | CHRM1 | 1 | |||||||
| snx-5422 | DICER1 | HSP90AA1 | 1 | |||||||
| sorafenib tosylate, valproic acid, sildenafil citrate | DICER1 | HDAC2 | 1 | |||||||
| sorafenib tosylate, valproic acid, sildenafil citrate | DICER1 | HDAC9 | 1 | |||||||
| sorafenib tosylate, valproic acid, sildenafil citrate | DICER1 | PPARD | 1 | |||||||
| tamoxifen, etoposide | DICER1 | PRKCA | 1 | |||||||
| temozolomide, aprepitant, minocycline, disulfiram, celecoxib, sertraline, captopril, itraconazole, ritonavir, auranofin | DICER1 | IL1B | 1 | |||||||
| temozolomide, depatuxizumab mafodotin, radiation, placebo for abt-414 | DICER1 | TUBB | 1 | |||||||
| temozolomide, lomustine, regorafenib, radiation, paxalisib, val-083, vt1021, troriluzole, adi-peg 20 | DICER1 | DDR2 | 1 | |||||||
| tinzaparin, tinzaparin | DICER1 | ITGA4 | 1 | |||||||
| trametinib, vinblastine | DICER1 | TUBB | 1 | |||||||
| valproic acid | DICER1 | HDAC2 | 1 | |||||||
| valproic acid | DICER1 | HDAC9 | 1 | |||||||
| valproic acid | DICER1 | PPARD | 1 | |||||||
| valproic acid, bevacizumab, radiation therapy | DICER1 | HDAC2 | 1 | |||||||
| valproic acid, bevacizumab, radiation therapy | DICER1 | HDAC9 | 1 | |||||||
| valproic acid, bevacizumab, radiation therapy | DICER1 | PPARD | 1 | |||||||
| valproic acid, simvastatin 20mg, gemcitabine 1000 mg, nab paclitaxel, cisplatin, capecitabine | DICER1 | HDAC2 | 1 | |||||||
| valproic acid, simvastatin 20mg, gemcitabine 1000 mg, nab paclitaxel, cisplatin, capecitabine | DICER1 | HDAC9 | 1 | |||||||
| valproic acid, simvastatin 20mg, gemcitabine 1000 mg, nab paclitaxel, cisplatin, capecitabine | DICER1 | PPARD | 1 | |||||||
| vinorelbine, xr9576 | DICER1 | TUBB | 1 | |||||||
| vorinostat, bevacizumab | DICER1 | HDAC2 | 1 | |||||||
| vorinostat, bevacizumab, irinotecan | DICER1 | HDAC2 | 1 | |||||||
| vorinostat, bortezomib, pharmacological study, laboratory biomarker analysis | DICER1 | HDAC2 | 1 | |||||||
| vorinostat, conventional surgery | DICER1 | HDAC2 | 1 | |||||||
| vorinostat, temozolomide, diagnostic laboratory biomarker analysis, pharmacological study | DICER1 | HDAC2 | 1 | |||||||
| vorinostat, temozolomide, magnetic resonance spectroscopic imaging, survey administration | DICER1 | HDAC2 | 1 | |||||||
| vorinostat, therapeutic conventional surgery, bortezomib | DICER1 | HDAC2 | 1 | |||||||
| acetylcholine | DICER1 | CHRM1 | 7 | |||||||
| acetylcholine chloride | DICER1 | CHRM1 | 7 | |||||||
| acitretin | DICER1 | RARB | 7 | |||||||
| adapalene | DICER1 | RARB | 7 | |||||||
| alitretinoin | DICER1 | RARB | 7 | |||||||
| alpidem | DICER1 | TSPO | 7 | |||||||
| anisotropine | DICER1 | CHRM1 | 7 | |||||||
| anisotropine methylbromide | DICER1 | CHRM1 | 7 | |||||||
| atropine | DICER1 | CHRM1 | 7 | |||||||
| atropine sulfate | DICER1 | CHRM1 | 7 | |||||||
| belantamab mafodotin | DICER1 | TUBB | 7 | |||||||
| belinostat | DICER1 | HDAC2 | 7 | |||||||
| belinostat | DICER1 | HDAC7 | 7 | |||||||
| belinostat | DICER1 | HDAC9 | 7 | |||||||
| belinostat | DICER1 | HDAC4 | 7 | |||||||
| benoxaprofen | DICER1 | ALOX12 | 7 | |||||||
| benztropine | DICER1 | CHRM1 | 7 | |||||||
| benztropine mesylate | DICER1 | CHRM1 | 7 | |||||||
| bethanechol chloride | DICER1 | CHRM1 | 7 | |||||||
| bexarotene | DICER1 | RARB | 7 | |||||||
| bezafibrate | DICER1 | PPARD | 7 | |||||||
| biperiden | DICER1 | CHRM1 | 7 | |||||||
| biperiden hydrochloride | DICER1 | CHRM1 | 7 | |||||||
| biperiden lactate | DICER1 | CHRM1 | 7 | |||||||
| cabazitaxel | DICER1 | TUBB | 7 | |||||||
| cevimeline | DICER1 | CHRM1 | 7 | |||||||
| cevimeline hydrochloride | DICER1 | CHRM1 | 7 | |||||||
| clidinium | DICER1 | CHRM1 | 7 | |||||||
| clidinium bromide | DICER1 | CHRM1 | 7 | |||||||
| clofarabine | DICER1 | RRM2 | 7 | |||||||
| cyclopentolate | DICER1 | CHRM1 | 7 | |||||||
| cyclopentolate hydrochloride | DICER1 | CHRM1 | 7 | |||||||
| cycrimine | DICER1 | CHRM1 | 7 | |||||||
| cycrimine hydrochloride | DICER1 | CHRM1 | 7 | |||||||
| dasatinib | DICER1 | SRC | 7 | |||||||
| dicyclomine | DICER1 | CHRM1 | 7 | |||||||
| dicyclomine hydrochloride | DICER1 | CHRM1 | 7 | |||||||
| diphemanil | DICER1 | CHRM1 | 7 | |||||||
| diphemanil methylsulfate | DICER1 | CHRM1 | 7 | |||||||
| diphenidol | DICER1 | CHRM1 | 7 | |||||||
| diphenidol hydrochloride | DICER1 | CHRM1 | 7 | |||||||
| docetaxel | DICER1 | TUBB | 7 | |||||||
| doxapram | DICER1 | KCNK3 | 7 | |||||||
| doxapram hydrochloride | DICER1 | KCNK3 | 7 | |||||||
| enasidenib | DICER1 | IDH2 | 7 | |||||||
| enasidenib mesylate | DICER1 | IDH2 | 7 | |||||||
| eribulin | DICER1 | TUBB | 7 | |||||||
| eribulin mesylate | DICER1 | TUBB | 7 | |||||||
| ethopropazine | DICER1 | CHRM1 | 7 | |||||||
| ethopropazine hydrochloride | DICER1 | CHRM1 | 7 | |||||||
| etretinate | DICER1 | RARB | 7 | |||||||
| fesoterodine | DICER1 | CHRM1 | 7 | |||||||
| fesoterodine fumarate | DICER1 | CHRM1 | 7 | |||||||
| flavoxate | DICER1 | CHRM1 | 7 | |||||||
| flavoxate | DICER1 | PDE7B | 7 | |||||||
| flavoxate | DICER1 | PDE7A | 7 |