MFHAS1

Fumarate hydratase, mitochondrial UniProt accession P07954

Catalyzes the reversible stereospecific interconversion of fumarate to L-malate (PubMed:30761759). Experiments in other species have demonstrated that specific isoforms of this protein act in defined pathways and favor one direction over the other (Probable)

Source: UniProt

Homotetramer (PubMed:21445611, PubMed:30761759). Interacts with H2AZ1 (PubMed:26237645)

Source: UniProt
Mitochondrion Cytoplasm, cytosol, Nucleus, Chromosome
Source: UniProt

Expressed in red blood cells; underexpressed in red blood cells (cytoplasm) of patients with hereditary non-spherocytic hemolytic anemia of unknown etiology

Source: UniProt
  • Fumarase deficiency (FMRD)

    A severe autosomal recessive metabolic disorder characterized by early-onset hypotonia, profound psychomotor retardation, and brain abnormalities, such as agenesis of the corpus callosum, gyral defects, and ventriculomegaly. Many patients show neonatal distress, metabolic acidosis, and/or encephalopathy.

  • Hereditary leiomyomatosis and renal cell cancer (HLRCC)

    A disorder characterized by predisposition to cutaneous and uterine leiomyomas, and papillary type 2 renal cancer which occurs in about 20% of patients.

Source: UniProt

Click a pathway to open the interactive Reactome viewer.

Pathway list and interactive viewer: Reactome

Synthetic Lethal Network

Genes with an experimentally identified or computationally predicted synthetic-lethal relationship to MFHAS1, aggregated across our SSL data sources. Click any partner node to view that gene’s page.

Nodes and edges are coloured by the SSL data source. Partners appearing in more than one source are shown in grey.

BioGRID SLOrth SynLethDB MexDrugs Multi-source
Sources: BioGRID, SLOrth, SynLethDB, MexDrugs

Clinical Trials

Total Trials Found: 1

NCT ID Condition Brief Title Phase Status
NCT05284513 Familial Hypercholesterolemia Collaborative Approach to Reach Everyone With Familial Hypercholesterolemia (CARE-FH) NA ENROLLING_BY_INVITATION
NCT00475826 Heterozigous Familial Hypercholesterolemia Evaluation of Chylomicrons Metabolism in Sub-Clinical Atherosclerosis in Patients Whit Heterozigous Familial Hypercholesterolemia (FH) Treated With Statin Plus Ezetimibe NA UNKNOWN
NCT01536080 Reflux Esophagitis (RE), Non-erosive Reflux Disease (NERD), Functional Heartburn (FH) Analysis of GERD Symptoms Using Gastroesophageal Reflux Impact Score Questionnaire for Quality of Life N/A COMPLETED
NCT06461702 Familial Hypercholesterolemia Clinical Exploration Trial of YOLT-101 in the Treatment of Familial Hypercholesterolemia (FH) EARLY_PHASE1 UNKNOWN
NCT01797939 Erosive Reflux Disease, Non-erosive Reflux Disease, Functional Heartburn Predictors of Proton Pump Inhibitor Response in Gastroesophageal Reflux Disease Patients N/A COMPLETED
NCT06043713 Metastatic Malignant Solid Neoplasm Autologous CD8+ and CD4+ Transgenic T Cells Expressing High Affinity KRASG12V Mutation-Specific T Cell Receptors (FH-A11KRASG12V-TCR) in Treating Patients With Metastatic Solid Tumor Cancers With KRAS G12V Mutations PHASE1 RECRUITING
NCT05043181 Familial Hypercholesterolemia Exosome-based Nanoplatform for Ldlr mRNA Delivery in FH PHASE1 NOT_YET_RECRUITING
NCT05238519 Familial Hypercholesterolemia, Cholesterol, Elevated, Genetic Disease Improved Diagnosis of Familial Hypercholesterolemia Across the Northland (ID-FH) PHASE3 ACTIVE_NOT_RECRUITING
NCT07427472 Heterozygous Familial Hypercholesterolemia (HeFH) "Detection and Follow-up of Coronary Lesions in HeFH (DESTINY-FH Study)" NA NOT_YET_RECRUITING
NCT04941599 Familial Hypercholesterolemia 2-Hydroxybenzylamine (2-HOBA) to Reduce HDL Modification and Improve HDL Function in Familial Hypercholesterolemia (FH) PHASE2 RECRUITING